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儿童脊髓性肌萎缩症的疾病修正治疗进展
诸丹蕙, 颜悦, 毛姗姗
Progress in disease-modifying theraies for spinal muscular atrophy in children
Danhui ZHU, Yue YAN, Shanshan MAO
临床药物治疗杂志 . 2025, (9): 8 -14 .  DOI: 10.3969/j.issn.1672-3384.2025.09.002