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黏多糖贮积症Ⅰ型患儿酶替代治疗一例
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Enzyme replacement therapy in child with mucopolysaccharidoses : a case report
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临床药物治疗杂志 . 2022, (5): 72 -74 .  DOI: 10.3969/j.issn.1672-3384.2022.05.014