疾病修正治疗药物用于儿童脊髓性肌萎缩症的临床综合评价
刘晓玲, 尉耘翠, 曹旺, 赵琴, 郭嘉亮, 阳创, 周晓梅, 何冠兰, 刘彦会, 赵华伟, 王钰, 郭吉芬, 马明健, 黄春芝, 王秀玲, 刘倩, 谢国权, 余静洁, 刘婷, 杨赛, 王晓玲
Clinical comprehensive evaluation of disease-modifying therapeutic drugs for spinal muscular atrophy in children
Xiaoling LIU, Yuncui YU, Wang CAO, Qin ZHAO, Jialiang GUO, Chuang YANG, Xiaomei ZHOU, Guanlan HE, Yanhui LIU, Huawei ZHAO, Yu WANG, Jifen GUO, Mingjian MA, Chunzhi HUANG, Xiuling WANG, Qian LIU, Guoquan XIE, Jingjie YU, Ting LIU, Sai YANG, Xiaoling WANG
临床药物治疗杂志
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2025, (3): 38
-47
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DOI: 10.3969/j.issn.1672-3384.2025.03.007